Abeona Therapeutics 2016 Investor Presentation Gene Therapy

Abeona Therapeutics is a rare disease-focused biotech company developing gene therapies for lysosomal storage diseases and epidermolysis bullosa. The company has three Phase I/II clinical programs including ABO-102 for Sanfilippo syndrome Type A and proprietary AAV vector technology enabling blood-brain barrier delivery via intravenous administration.